Neuromuscular · Rare · teaser

Spinal muscular atrophy

Updated August 2026 · SMN1 (5q)

Teaser case. Selected price and peak-sales fields are held for a paid Brief — the rest is the method.

Model levers

Custom per indication. These sliders re-cut the published funnel — they do not invent a claims extract.

Funnel · US

Prevalent SMA9,500

Diagnosed / in care8,200

Type 1 (incident-like)1,100

Type 22,800

Type 3 / 44,300

On SMN-modifying Rx6,400

GT-eligible incident420

Clinical type

  • Type 114%
  • Type 234%
  • Type 3 / 452%

SMN2

  • 2 SMN2 copies20%
  • 3 SMN2 copies48%
  • ≥4 SMN2 copies32%